Inés, a 3-year-old girl diagnosed with the rare disease BPAN, urgently needs 11 million euros to fund a gene therapy that could stop her neurodegeneration, as the damage she suffers is irreversible over time. #EnfermedadRara #BPAN #InvestigaciónMédica (translated)
La esperanza para Inés, con una enfermedad rara, cuesta 11 millones: "No podemos permitir que se pare la investigación"
