Investigadores de las universidades Wake Forest, Duke y Wisconsin-Madison han identificado en un estudio publicado en PNAS los genes SP6 y SP8, responsables de la regeneración de extremidades en ajolotes, ratones y peces cebra, abriendo nuevas posibilidades en la medicina regenerativa y la terapia génica para tratar la pérdida de extremidades en humanos. #Hantavirus #RegenerativeMedicine #GeneTherapy

The U.S. military has already conducted a clinical trial with an injection of DNA gene therapy of the Andes variant of hantavirus — the exact same variant that caused the outbreak on the cruise ship. 98% of participants experienced adverse events. The plasmid. (Original: L'armée américaine a déjà mené un essai clinique avec une injection de thérapie génique à ADN du variant Andes du hantavirus — le même variant exact à l'origine de l'épidémie sur le navire de croisière. 98 % des participants ont subi des événements indésirables. Le plasmide) #GeneTherapy #Hantavirus #ClinicalTrial #US
Il presidente della Fondazione Cutino, Aurelio Maggio, annuncia che grazie alla terapia genica per la talassemia, per la prima volta si può parlare di guarigione definitiva, segnando un'epoca di cambiamento nella gestione della patologia in Sicilia, dove già sono stati selezionati i primi pazienti per il trattamento. #Thalassemia #GeneTherapy #HealthcareInnovation

Pam Belluck's article highlights the experience of Amanda Sifford, an A.L.S. patient undergoing the newly approved therapy tofersen in Miami, which has led to notable improvements in her breathing and mobility, raising hope for others with this debilitating disease despite its severe side effects and the challenges of treating various A.L.S. symptoms. #ALS #NeurodegenerativeDisorders #GeneTherapy #US #CA

American biotechnology company Regeneron has developed a groundbreaking gene therapy called Otarmeni to treat a rare genetic form of deafness, which has shown significant auditory improvement in at least 80% of 20 pediatric patients tested, and is set to be offered for free to eligible patients, marking a pivotal advance in treating genetic hearing loss. #GeneTherapy #HearingLoss #Biotechnology

In a significant milestone for the treatment of epidermolysis bullosa, two Andalusian patients, Leo and Adrián, have become the first in Spain to receive gene therapy with the drug Vyjuvek, promising to greatly improve their quality of life by reducing pain and healing time, although challenges remain regarding equitable access to this life-changing treatment across the country. #GeneTherapy #HealthEquity #RareDiseases #ES #ES #ES #ES









