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#NEDAMSS

Elenita, a 9-year-old girl from Granada with NEDAMSS, has raised 1.6 million euros to bring a gene therapy to Spain that could halt her ultra-rare neurodegenerative disease and restore lost abilities. #Elenita #NEDAMSS #TerapiaGenética (translated)

Elenita, la niña que ha logrado recaudar 1,6 millones para traer a España una terapia génica: "Estamos muy esperanzados"